Nóbrega, ClévioMendonca, L. S.Marcelo, AdrianaLamaziere, A.Tome, S.Despres, G.Matos, C.Mechmet, FatichLangui, D.den Dunnen, W.de Almeida, L. P.Cartier, N.Alves, S.2020-05-042020-05-042020http://hdl.handle.net/10400.1/13824Aims/Context: Machado-Joseph Disease (MJD) is a neurodegenerative disease associated with extensive neuronal death. Defects in brain cholesterol metabolism may contribute to neurodegenerative diseases.engGene therapyconference object10.1097/MD.0000000000019291